• 8857 Citations
  • 42 h-Index
1987 …2019
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Fingerprint Dive into the research topics where Giuliana Ferrari is active. These topic labels come from the works of this person. Together they form a unique fingerprint.

  • 29 Similar Profiles
Genetic Therapy Medicine & Life Sciences
Hematopoietic Stem Cells Medicine & Life Sciences
Genes Medicine & Life Sciences
Thalassemia Medicine & Life Sciences
Bone Marrow Medicine & Life Sciences
Globins Medicine & Life Sciences
Stem Cells Medicine & Life Sciences
Gene therapy Chemical Compounds

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Research Output 1987 2019

  • 8857 Citations
  • 42 h-Index
  • 79 Article
  • 1 Letter
1 Citation (Scopus)
Open Access
Thalassemia
Mesenchymal Stromal Cells
Bone Marrow
Iron Overload
Hematopoietic Stem Cells
11 Citations (Scopus)

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Marktel, S., Scaramuzza, S., Cicalese, M. P., Giglio, F., Galimberti, S., Lidonnici, M. R., Calbi, V., Assanelli, A., Bernardo, M. E., Rossi, C., Calabria, A., Milani, R., Gattillo, S., Benedicenti, F., Spinozzi, G., Aprile, A., Bergami, A., Casiraghi, M., Consiglieri, G., Masera, N. & 18 others, D’Angelo, E., Mirra, N., Origa, R., Tartaglione, I., Perrotta, S., Winter, R., Coppola, M., Viarengo, G., Santoleri, L., Graziadei, G., Gabaldo, M., Valsecchi, M. G., Montini, E., Naldini, L., Cappellini, M. D., Ciceri, F., Aiuti, A. & Ferrari, G., Jan 1 2019, (Accepted/In press) In : Nature Medicine.

Research output: Contribution to journalArticle

Gene therapy
Pediatrics
Thalassemia
Cell- and Tissue-Based Therapy
Hematopoietic Stem Cells

Gene therapy and gene editing strategies for hemoglobinopathies

Lidonnici, MR. & Ferrari, G., 2018, In : Blood Cells, Molecules, and Diseases. 70, 6, p. 87-101 15 p.

Research output: Contribution to journalArticle

Hemoglobinopathies
Globins
Genetic Therapy
Thalassemia
Sickle Cell Anemia

Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-Thalassemia

Lidonnici, MR., Paleari, Y., Tiboni, F., Mandelli, G., Rossi, C., Vezzoli, M., Aprile, A., Lederer, CW., Ambrosi, A., Chanut, F., Sanvito, F., Calabria, A., Poletti, V., Mavilio, F., Montini, E., Naldini, L., Cristofori, P. & Ferrari, G., 2018, In : Molecular Therapy - Methods and Clinical Development. 11, p. 9-28 20 p.

Research output: Contribution to journalArticle

Lentivirus
Thalassemia
Genetic Therapy
Hematopoietic Stem Cells
Safety

Transferrin receptor 2 is a potential novel therapeutic target for β-thalassemia: evidence from a murine model

Artuso, I., Lidonnici, MR., Altamura, S., Mandelli, G., Pettinato, M., Muckenthaler, MU., Silvestri, L., Ferrari, G., Camaschella, C. & Nai, A., 2018, In : Blood. 132, 21, p. 2286-2297 12 p.

Research output: Contribution to journalArticle

Transferrin Receptors
Thalassemia
Iron Overload
Anemia
Erythropoiesis