• 38144 Citations
  • 93 h-Index
1980 …2019
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Fingerprint Dive into the research topics where Luigi Naldini is active. These topic labels come from the works of this person. Together they form a unique fingerprint.

  • 39 Similar Profiles
Genetic Therapy Medicine & Life Sciences
Hematopoietic Stem Cells Medicine & Life Sciences
Genes Medicine & Life Sciences
Transgenes Medicine & Life Sciences
Gene therapy Chemical Compounds
MicroRNAs Medicine & Life Sciences
Gene transfer Chemical Compounds
Neoplasms Medicine & Life Sciences

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Research Output 1980 2019

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Marktel, S., Scaramuzza, S., Cicalese, M. P., Giglio, F., Galimberti, S., Lidonnici, M. R., Calbi, V., Assanelli, A., Bernardo, M. E., Rossi, C., Calabria, A., Milani, R., Gattillo, S., Benedicenti, F., Spinozzi, G., Aprile, A., Bergami, A., Casiraghi, M., Consiglieri, G., Masera, N. & 18 others, D’Angelo, E., Mirra, N., Origa, R., Tartaglione, I., Perrotta, S., Winter, R., Coppola, M., Viarengo, G., Santoleri, L., Graziadei, G., Gabaldo, M., Valsecchi, M. G., Montini, E., Naldini, L., Cappellini, M. D., Ciceri, F., Aiuti, A. & Ferrari, G., 2019, In : Nature Medicine. 25, 2, p. 234-241 8 p.

Research output: Contribution to journalArticle

18 Citations (Scopus)

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Marktel, S., Scaramuzza, S., Cicalese, M. P., Giglio, F., Galimberti, S., Lidonnici, M. R., Calbi, V., Assanelli, A., Bernardo, M. E., Rossi, C., Calabria, A., Milani, R., Gattillo, S., Benedicenti, F., Spinozzi, G., Aprile, A., Bergami, A., Casiraghi, M., Consiglieri, G., Masera, N. & 18 others, D’Angelo, E., Mirra, N., Origa, R., Tartaglione, I., Perrotta, S., Winter, R., Coppola, M., Viarengo, G., Santoleri, L., Graziadei, G., Gabaldo, M., Valsecchi, M. G., Montini, E., Naldini, L., Cappellini, M. D., Ciceri, F., Aiuti, A. & Ferrari, G., Jan 1 2019, (Accepted/In press) In : Nature Medicine.

Research output: Contribution to journalArticle

Gene therapy
Pediatrics
Thalassemia
Cell- and Tissue-Based Therapy
Hematopoietic Stem Cells
8 Citations (Scopus)

Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study

Ferrua, F., Cicalese, M. P., Galimberti, S., Giannelli, S., Dionisio, F., Barzaghi, F., Migliavacca, M., Bernardo, M. E., Calbi, V., Assanelli, A. A., Facchini, M., Fossati, C., Albertazzi, E., Scaramuzza, S., Brigida, I., Scala, S., Basso-Ricci, L., Pajno, R., Casiraghi, M., Canarutto, D. & 18 others, Salerio, F. A., Albert, M. H., Bartoli, A., Wolf, H. M., Fiori, R., Silvani, P., Gattillo, S., Villa, A., Biasco, L., Dott, C., Culme-Seymour, E. J., van Rossem, K., Atkinson, G., Valsecchi, M. G., Roncarolo, M. G., Ciceri, F., Naldini, L. & Aiuti, A., May 1 2019, In : The Lancet Haematology. 6, 5, p. e239-e253

Research output: Contribution to journalArticle

Open Access
Wiskott-Aldrich Syndrome
Cell- and Tissue-Based Therapy
Genetic Therapy
Stem Cells
Wiskott-Aldrich Syndrome Protein
12 Citations (Scopus)

Precise Gene Editing Preserves Hematopoietic Stem Cell Function following Transient p53-Mediated DNA Damage Response

Schiroli, G., Conti, A., Ferrari, S., della Volpe, L., Jacob, A., Albano, L., Beretta, S., Calabria, A., Vavassori, V., Gasparini, P., Salataj, E., Ndiaye-Lobry, D., Brombin, C., Chaumeil, J., Montini, E., Merelli, I., Genovese, P., Naldini, L. & Di Micco, R., Apr 4 2019, In : Cell Stem Cell. 24, 4, p. 551-565.e8

Research output: Contribution to journalArticle

Open Access
Hematopoietic Stem Cells
DNA Damage
Gene Editing
Clustered Regularly Interspaced Short Palindromic Repeats
Dependovirus
Mucopolysaccharidosis I
Iduronidase
Transgenes
Genetic Therapy
Hematopoietic Stem Cells