If you made any changes in Pure these will be visible here soon.

Research Output 1973 2020

2020

Iron deficiency anaemia revisited

Cappellini, M. D., Musallam, K. M. & Taher, A. T., 2020, In : Journal of Internal Medicine. 287, 2, p. 153-170

Research output: Contribution to journalReview article

Open Access
Iron-Deficiency Anemias
Ferritins
Iron
Transferrin
Serum

Management of age-associated medical complications in patients with β-thalassemia

Motta, I., Mancarella, M., Marcon, A., Vicenzi, M. & Cappellini, M. D., 2020, In : Expert Review of Hematology. 13, 1, p. 85-94

Research output: Contribution to journalReview article

Thalassemia
Expert Testimony
Adrenal Insufficiency
Kidney Neoplasms
Bone Diseases
2019
Fetal Hemoglobin
Thalassemia
Codon
Single Nucleotide Polymorphism
Phenotype

Current challenges in the management of patients with sickle cell disease - A report of the Italian experience

Russo, G., De Franceschi, L., Colombatti, R., Rigano, P., Perrotta, S., Voi, V., Palazzi, G., Fidone, C., Quota, A., Graziadei, G., Pietrangelo, A., Pinto, V., Ruffo, G. B., Sorrentino, F., Venturelli, D., Casale, M., Ferrara, F., Sainati, L., Cappellini, M. D., Piga, A. & 2 others, Maggio, A. & Forni, G. L., May 30 2019, In : Orphanet Journal of Rare Diseases. 14, 1, 120.

Research output: Contribution to journalArticle

Open Access
Sickle Cell Anemia
Hemoglobinopathies
Mediterranean Region
Sickle Hemoglobin
Middle East

Development of a patient-reported outcomes symptom measure for patients with nontransfusion-dependent thalassemia (NTDT-PRO©)

Taher, A., Viprakasit, V., Cappellini, M. D., Sutcharitchan, P., Ward, R., Mahmoud, D., Laadem, A., Khan, A., Gwaltney, C., Harding, G., Attie, K., Zhang, X., Zou, J., Pariseau, J., Hu, X. H. & Kattamis, A., 2019, In : American Journal of Hematology. 94, 2, p. 171-176

Research output: Contribution to journalArticle

Thalassemia
Lebanon
Greece
Interviews
United States Food and Drug Administration

Development of a thalassemia-related thrombosis risk scoring system

Taher, A. T., Cappellini, M. D. & Musallam, K. M., Jan 1 2019, In : American Journal of Hematology. 94, 8, p. E207-E209

Research output: Contribution to journalLetter

Open Access

Diagnosis of chronic anaemia in gastrointestinal disorders: A guideline by the Italian Association of Hospital Gastroenterologists and Endoscopists (AIGO) and the Italian Society of Paediatric Gastroenterology Hepatology and Nutrition (SIGENP)

Elli, L., Norsa, L., Zullo, A., Carroccio, A., Girelli, C., Oliva, S., Romano, C., Leandro, G., Bellini, M., Marmo, R., Soncini, M., Monica, F., De Francesco, V., Paulon, E., Cappellini, M. D., Motta, I., Ferretti, F., Orlando, S., Mansueto, P., Buscarini, E. & 4 others, Manfredi, G., Agostoni, C., Tomba, C. & Cannizzaro, R., Apr 1 2019, In : Digestive and Liver Disease. 51, 4, p. 471-483 13 p.

Research output: Contribution to journalReview article

Gastroenterology
Anemia
Guidelines
Pediatrics
Gastroenterologists

Diagnosis of chronic anaemia in gastrointestinal disorders: A guideline by the Italian Association of Hospital Gastroenterologists and Endoscopists (AIGO) and the Italian Society of Paediatric Gastroenterology Hepatology and Nutrition (SIGENP)

Elli, L., Norsa, L., Zullo, A., Carroccio, A., Girelli, C., Oliva, S., Romano, C., Leandro, G., Bellini, M., Marmo, R., Soncini, M., Monica, F., De Francesco, V., Paulon, E., Cappellini, M. D., Motta, I., Ferretti, F., Orlando, S., Mansueto, P., Buscarini, E. & 4 others, Manfredi, G., Agostoni, C., Tomba, C. & Cannizzaro, R., Apr 2019, In : Digestive and Liver Disease. 51, 4, p. 471-483 13 p.

Research output: Contribution to journalArticle

Gastroenterology
Anemia
Guidelines
Pediatrics
Gastroenterologists

EXPLORE: A Prospective, Multinational, Natural History Study of Patients with Acute Hepatic Porphyria with Recurrent Attacks

Gouya, L., Ventura, P., Balwani, M., Bissell, D. M., Rees, D. C., Stölzel, U., Phillips, J. D., Kauppinen, R., Langendonk, J. G., Desnick, R. J., Deybach, J. C., Bonkovsky, H. L., Parker, C., Naik, H., Badminton, M., Stein, P. E., Minder, E., Windyga, J., Bruha, R., Cappellini, M. D. & 16 others, Sardh, E., Harper, P., Sandberg, S., Aarsand, A. K., Andersen, J., Alegre, F., Ivanova, A., Talbi, N., Chan, A., Querbes, W., Ko, J., Penz, C., Liu, S., Lin, T., Simon, A. & Anderson, K. E., Jan 1 2019, (Accepted/In press) In : Hepatology.

Research output: Contribution to journalArticle

Open Access
Natural History
Hemin
Aminolevulinic Acid
Health Facilities
Acute Hepatic Porphyria
Open Access

Hospital Care of Older Patients With COPD: Adherence to International Guidelines for Use of Inhaled Bronchodilators and Corticosteroids

REPOSI investigators, Proietti, M., Agosti, P., Lonati, C., Corrao, S., Perticone, F., Mannucci, P. M., Nobili, A. & Harari, S., Jan 1 2019, In : Journal of the American Medical Directors Association. 20, 10, p. 1313-1317.e9

Research output: Contribution to journalArticle

Bronchodilator Agents
Chronic Obstructive Pulmonary Disease
Patient Care
Adrenal Cortex Hormones
Guidelines

International Porphyria Molecular Diagnostic Collaborative: an evidence-based database of verified pathogenic and benign variants for the porphyrias

Chen, B., Whatley, S., Badminton, M., Aarsand, A. K., Anderson, K. E., Bissell, D. M., Bonkovsky, H. L., Cappellini, M. D., Floderus, Y., Friesema, E. C. H., Gouya, L., Harper, P., Kauppinen, R., Loskove, Y., Martásek, P., Phillips, J. D., Puy, H., Sandberg, S., Schmitt, C., To-Figueras, J. & 4 others, Weiss, Y., Yasuda, M., Deybach, J. C. & Desnick, R. J., Jan 1 2019, In : Genetics in Medicine. 21, 11, p. 2605-2613

Research output: Contribution to journalArticle

Porphyrias
Molecular Pathology
Databases
Virulence
Coproporphyrinogen Oxidase

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Marktel, S., Scaramuzza, S., Cicalese, M. P., Giglio, F., Galimberti, S., Lidonnici, M. R., Calbi, V., Assanelli, A., Bernardo, M. E., Rossi, C., Calabria, A., Milani, R., Gattillo, S., Benedicenti, F., Spinozzi, G., Aprile, A., Bergami, A., Casiraghi, M., Consiglieri, G., Masera, N. & 18 others, D’Angelo, E., Mirra, N., Origa, R., Tartaglione, I., Perrotta, S., Winter, R., Coppola, M., Viarengo, G., Santoleri, L., Graziadei, G., Gabaldo, M., Valsecchi, M. G., Montini, E., Naldini, L., Cappellini, M. D., Ciceri, F., Aiuti, A. & Ferrari, G., 2019, In : Nature Medicine. 25, 2, p. 234-241 8 p.

Research output: Contribution to journalArticle

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Marktel, S., Scaramuzza, S., Cicalese, M. P., Giglio, F., Galimberti, S., Lidonnici, M. R., Calbi, V., Assanelli, A., Bernardo, M. E., Rossi, C., Calabria, A., Milani, R., Gattillo, S., Benedicenti, F., Spinozzi, G., Aprile, A., Bergami, A., Casiraghi, M., Consiglieri, G., Masera, N. & 18 others, D’Angelo, E., Mirra, N., Origa, R., Tartaglione, I., Perrotta, S., Winter, R., Coppola, M., Viarengo, G., Santoleri, L., Graziadei, G., Gabaldo, M., Valsecchi, M. G., Montini, E., Naldini, L., Cappellini, M. D., Ciceri, F., Aiuti, A. & Ferrari, G., Jan 1 2019, (Accepted/In press) In : Nature Medicine.

Research output: Contribution to journalArticle

Gene therapy
Pediatrics
Thalassemia
Cell- and Tissue-Based Therapy
Hematopoietic Stem Cells

Iron overload in congenital haemolytic anaemias: role of hepcidin and cytokines and predictive value of ferritin and transferrin saturation

Barcellini, W., Zaninoni, A., Gregorini, A. I., Soverini, G., Duca, L., Fattizzo, B., Giannotta, J. A., Pedrotti, P., Vercellati, C., Marcello, A. P., Fermo, E., Bianchi, P. & Cappellini, M. D., May 1 2019, In : British Journal of Haematology. 185, 3, p. 523-531 9 p.

Research output: Contribution to journalArticle

Congenital Hemolytic Anemia
Hepcidins
Iron Overload
Transferrin
Ferritins
Open Access
beta-Thalassemia
Fertilization in Vitro
Oocytes
Anti-Mullerian Hormone
Embryonic Structures

Patterns of infections in older patients acutely admitted to medical wards: data from the REPOSI register

REPOSI investigators, Rossio, R., Ardoino, I., Franchi, C., Nobili, A., Mannuccio Mannucci, P. & Peyvandi, F., Jan 1 2019, In : Internal and Emergency Medicine. p. 1347-1352

Research output: Contribution to journalLetter

Prevalence of use and appropriateness of antidepressants prescription in acutely hospitalized elderly patients

REPOSI collaborators, Steering Committee, Clinical Data Monitoring and Revision, Database Management and Statistics & Investigators, Oct 1 2019, In : European Journal of Internal Medicine. 68, p. e7-e11

Research output: Contribution to journalLetter

Prevalence of use and appropriateness of antidepressants prescription in acutely hospitalized elderly patients

collaborators, REPOSI., Committee, S., Revision, C. D. M. A., Statistics, D. M. A., Abctctb, I., Carlotta, F., Raffaella, R., Ilaria, A., Mannucci, P. M., Nobili, A., Corazza, G. R., Salerno, F., Cesari, M., Tettamanti, M., Pasina, L., Cortesi, L., Bernardi, M., Barbagallo, M., Natoli, G., Cappellini, M. D. & 35 others, Fabio, G., De Amicis, M. M., De Luca, G., Rossi, P. D., Damanti, S., Di Sabatino, A., Miceli, E., Lenti, M. V., Murialdo, G., Carbone, M., Rizzo, M. R., Bracco, C., Fracanzani, A. L., Fargion, S., Sigon, G., Peyvandi, F., Monzani, V., Savojardo, V., Folli, C., Dallegri, F., Bianchi, G. B., Mirijello, A., Bertolotti, M., Mussi, C., Martino, G. P., Arcopinto, M., Marra, A. M., Ballestrero, A., Berti, F., Artoni, A., Porta, M., Tedeschi, A., Harari, S., Lonati, C. & Cattaneo, M., Oct 1 2019, In : European Journal of Internal Medicine. 68, p. e7-e11

Research output: Contribution to journalArticle

Quality of life in patients with β-thalassemia: A prospective study of transfusion-dependent and non-transfusion-dependent patients in Greece, Italy, Lebanon, and Thailand

Cappellini, M. D., Kattamis, A., Viprakasit, V., Sutcharitchan, P., Pariseau, J., Laadem, A., Jessent-Ciaravino, V. & Taher, A., Jan 1 2019, In : American Journal of Hematology. 94, 10, p. E261-E264

Research output: Contribution to journalLetter

Open Access

Red blood cell distribution width as a prognostic factor of mortality in elderly patients firstly hospitalized due to heart failure

Salvatori, M., Formiga, F., Moreno-Gónzalez, R., Chivite, D., De Amicis, M. M., Cappellini, M. D. & Corbella, X., Jan 1 2019, In : Kardiologia Polska. 77, 6, p. 632-638 7 p.

Research output: Contribution to journalArticle

Erythrocyte Indices
Heart Failure
Erythrocytes
Mortality
Tertiary Healthcare

Risk factors for heart disease in transfusion-dependent thalassemia: serum ferritin revisited

on behalf of Webthal®, Derchi, G., Dessì, C., Bina, P., Cappellini, M. D., Piga, A., Perrotta, S., Tartaglione, I., Giuditta, M., Longo, F., Origa, R., Quarta, A., Pinto, V. & Forni, G. L., 2019, In : Internal and Emergency Medicine. 14, 3, p. 365-370 6 p.

Research output: Contribution to journalArticle

Thalassemia
Ferritins
Heart Diseases
Serum
Iron Overload

Sotatercept, a novel transforming growth factor β ligand trap, improves anemia in β-thalassemia: A phase II, open-label, dose-finding study

Cappellini, M. D., Porter, J., Origa, R., Forni, G. L., Voskaridou, E., Galactéros, F., Taher, A. T., Arlet, J. B., Ribeil, J. A., Garbowski, M., Graziadei, G., Brouzes, C., Semeraro, M., Laadem, A., Miteva, D., Zou, J., Sung, V., Zinger, T., Attie, K. M. & Hermine, O., Feb 28 2019, In : Haematologica. 104, 3, p. 477-484 8 p.

Research output: Contribution to journalArticle

Open Access
Thalassemia
Transforming Growth Factors
Anemia
Ligands
Erythropoiesis

The autophagy-activating kinase ULK1 mediates clearance of free α-globin in β-thalassemia

Lechauve, C., Keith, J., Khandros, E., Fowler, S., Mayberry, K., Freiwan, A., Thom, C. S., Delbini, P., Romero, E. B., Zhang, J., Motta, I., Tillman, H., Cappellini, M. D., Kundu, M. & Weiss, M. J., Aug 21 2019, In : Science Translational Medicine. 11, 506, eaav4881.

Research output: Contribution to journalArticle

Thalassemia
Globins
Autophagy
Phosphotransferases
Sirolimus

Treatment with ferric carboxymaltose in stable patients with severe iron deficiency anemia in the emergency department

Motta, I., Mantovan, G., Consonni, D., Brambilla, A. M., Materia, M., Porzio, M., Migone De Amicis, M., Montano, N. & Cappellini, M. D., Jan 1 2019, (Accepted/In press) In : Internal and Emergency Medicine.

Research output: Contribution to journalArticle

Iron-Deficiency Anemias
Hospital Emergency Service
Therapeutics
Iron
ferric carboxymaltose

UGT1A1 genotype does not affect tyrosine kinase inhibitors efficacy and safety in chronic myeloid leukemia

Iurlo, A., Bucelli, C., Cattaneo, D., Levati, G. V., Viani, B., Tavazzi, D., Consonni, D., Baldini, L. & Cappellini, M. D., Jan 1 2019, In : American Journal of Hematology. 94, 11, p. E283-E285

Research output: Contribution to journalLetter

Open Access

Validation of a patient-reported outcomes symptom measure for patients with nontransfusion-dependent thalassemia (NTDT-PRO©)

Taher, A., Cappellini, M. D., Viprakasit, V., Sutcharitchan, P., Mahmoud, D., Laadem, A., Khan, A., Gwaltney, C., Harding, G., Attie, K., Zhang, X., Zou, J., Pariseau, J., Henry Hu, X. & Kattamis, A., 2019, In : American Journal of Hematology. 94, 2, p. 177-183

Research output: Contribution to journalArticle

Thalassemia
Dyspnea
Lebanon
Validation Studies
beta-Thalassemia

A paradigm shift on beta-thalassaemia treatment: How will we manage this old disease with new therapies?

Cappellini, M. D., Porter, J. B., Viprakasit, V. & Taher, A. T., 2018, In : Blood Reviews. 32, 4, p. 300-311

Research output: Contribution to journalArticle

beta-Thalassemia
Therapeutics
Erythropoiesis
Hematopoietic Stem Cell Transplantation
Hemolytic Anemia

Choice and Outcomes of Rate Control versus Rhythm Control in Elderly Patients with Atrial Fibrillation: A Report from the REPOSI Study

REPOSI investigators, 2018, In : Drugs and Aging. 35, 5, p. 365-373 9 p.

Research output: Contribution to journalArticle

Atrial Fibrillation
Polypharmacy
Odds Ratio
Confidence Intervals
Cause of Death

Circulating cell-free DNA and ineffective erythropoiesis in nontransfusion-dependent β-thalassemia

Tavazzi, D., Motta, I., Graziadei, G., Sampietro, M., Duca, L. & Cappellini, M. D., 2018, In : American Journal of Hematology. 93, 11, p. E365-E368

Research output: Contribution to journalArticle

Clinical Complications and Their Management

Marcon, A., Motta, I., Taher, A. T. & Cappellini, M. D., Apr 1 2018, In : Hematology/Oncology Clinics of North America. 32, 2, p. 223-236 14 p.

Research output: Contribution to journalReview article

Thalassemia
Erythropoiesis
Hemolysis
Blood Transfusion
Phenotype

Clinical outcomes of Clostridium difficile infection according to strain type. A prospective study in medical wards

Serafino, S., Consonni, D., Migone De Amicis, M., Sisto, F., Domeniconi, G., Formica, S., Zarantonello, M., Maraschini, A., Cappellini, M. D., Spigaglia, P., Barbanti, F., Castaldi, S. & Fabio, G., 2018, In : European Journal of Internal Medicine. 54, p. 21-26

Research output: Contribution to journalArticle

Clostridium Infections
Clostridium difficile
Prospective Studies
Ribotyping
Italy

Finding and treating gaucher disease type 1 - The role of the haematologist

Cappellini, M. D., Cassinerio, E., Motta, I., Morello, W. & Villarubia, J., Jun 1 2018, In : European Oncology and Haematology. 14, 1, p. 50-56 7 p.

Research output: Contribution to journalArticle

Gaucher Disease
Splenomegaly
Thrombocytopenia
Lysosomal Storage Diseases
Enzyme Replacement Therapy

How I manage medical complications of b-thalassemia in adults

Taher, A. T. & Cappellini, M. D., Oct 25 2018, In : Blood. 132, 17, p. 1781-1791 11 p.

Research output: Contribution to journalArticle

Thalassemia
Iron
Morbidity
Iron Overload
Erythropoiesis

Hypercoagulability and Vascular Disease

Taher, A. T., Cappellini, M. D., Bou-Fakhredin, R., Coriu, D. & Musallam, K. M., Apr 1 2018, In : Hematology/Oncology Clinics of North America. 32, 2, p. 237-245 9 p.

Research output: Contribution to journalReview article

Thalassemia
Thrombophilia
Vascular Diseases
Incidence

Low-dose Synachten test with measurement of salivary cortisol in adult patients with β-thalassemia major

Ambrogio, A. G., Danesi, L., Baldini, M., Radin, R., Cassinerio, E., Graziadei, G., Mirra, N., D'Angelo, E., Marcon, A., Mancarella, M., Orsatti, A., Bonetti, F., Scacchi, M., Cappellini, M. D., Persani, L. & Pecori Giraldi, F., May 2018, In : Endocrine. 60, 2, p. 348-354 7 p.

Research output: Contribution to journalArticle

Low-dose Synachten test with measurement of salivary cortisol in adult patients with β-thalassemia major

Ambrogio, A. G., Danesi, L., Baldini, M., Radin, R., Cassinerio, E., Graziadei, G., Mirra, N., D’Angelo, E., Marcon, A., Mancarella, M., Orsatti, A., Bonetti, F., Scacchi, M., Cappellini, M. D., Persani, L. & Pecori Giraldi, F., 2018, In : Endocrine. 60, 2, p. 348-354 7 p.

Research output: Contribution to journalArticle

beta-Thalassemia
Hydrocortisone
Adrenocorticotropic Hormone
Serum
Congenital, Hereditary, and Neonatal Diseases and Abnormalities

Low-dose Synachten test with measurement of salivary cortisol in adult patients with β-thalassemia major

Ambrogio, A. G., Danesi, L., Baldini, M., Radin, R., Cassinerio, E., Graziadei, G., Mirra, N., D'Angelo, E., Marcon, A., Mancarella, M., Orsatti, A., Bonetti, F., Scacchi, M., Cappellini, M. D., Persani, L. & Pecori Giraldi, F., May 2018, In : Endocrine. 60, 2, p. 348-354 7 p.

Research output: Contribution to journalArticle

beta-Thalassemia
Hydrocortisone
Adrenocorticotropic Hormone
Serum
Congenital, Hereditary, and Neonatal Diseases and Abnormalities

Microcytosis is important in screening of iron deficiency anemia

De Franceschi, L., Iolascon, A., Taher, A. & Cappellini, M. D., Feb 1 2018, In : European Journal of Internal Medicine. 48, p. e39

Research output: Contribution to journalLetter

Non-transferrin-bound iron and oxidative stress during allogeneic hemopoietic stem cell transplantation in patients with or without iron overload

Duca, L., Cappellini, M. D., Baronciani, D., Pilo, F., Targhetta, C., Visani, G., Nava, I. & Angelucci, E., 2018, In : American Journal of Hematology. 93, 9, p. E250-E252 3 p.

Research output: Contribution to journalArticle

Non-transfusion-dependent thalassemia: An update on complications and management

Sleiman, J., Tarhini, A., Bou-Fakhredin, R., Saliba, A. N., Cappellini, M. D. & Taher, A. T., Jan 8 2018, In : International Journal of Molecular Sciences. 19, 1, 182.

Research output: Contribution to journalReview article

Thalassemia
Iron
liver
iron
Liver

Polypharmacy in older people: lessons from 10 years of experience with the REPOSI register

REPOSI Collaborators (REPOSI is the acronym of REgistro POliterapie SIMI, Società Italiana di Medicina Interna), 2018, In : Internal and Emergency Medicine. 13, 8, p. 1191-1200

Research output: Contribution to journalArticle

Polypharmacy
Prescriptions
Internal Medicine
Geriatrics
Population

Prevalence and predictors of liver fibrosis evaluated by vibration controlled transient elastography in type 1 Gaucher disease

Nascimbeni, F., Cassinerio, E., Dalla Salda, A., Motta, I., Bursi, S., Donatiello, S., Spina, V., Cappellini, M. D. & Carubbi, F., 2018, In : Molecular Genetics and Metabolism. 125, 1-2, p. 64-72

Research output: Contribution to journalArticle

Elasticity Imaging Techniques
Gaucher Disease
Vibration
Liver Cirrhosis
Liver

Real-life experience with hydroxyurea in sickle cell disease: A multicenter study in a cohort of patients with heterogeneous descent

Rigano, P., De Franceschi, L., Sainati, L., Piga, A., Piel, F. B., Cappellini, M. D., Fidone, C., Masera, N., Palazzi, G., Gianesin, B. & Forni, G. L., 2018, In : Blood Cells, Molecules, and Diseases. 69, p. 82-89

Research output: Contribution to journalArticle

Hydroxyurea
Sickle Cell Anemia
Multicenter Studies
Therapeutics
Acute Chest Syndrome

Role of T1 mapping as a complementary tool to T2* for non-invasive cardiac iron overload assessment

Torlasco, C., Cassinerio, E., Roghi, A., Faini, A., Capecchi, M., Abdel-Gadir, A., Giannattasio, C., Parati, G., Moon, J. C., Cappellini, M. D. & Pedrotti, P., 2018, In : PLoS One. 13, 2, p. e0192890

Research output: Contribution to journalArticle

iron overload
Iron Overload
Iron
iron
thalassemia

Role of T1 mapping as a complementary tool to T2 for non-invasive cardiac iron overload assessment

Torlasco, C., Cassinerio, E., Roghi, A., Faini, A., Capecchi, M., Abdel-Gadir, A., Giannattasio, C., Parati, G., Moon, J. C., Cappellini, M. D. & Pedrotti, P., Feb 1 2018, In : PLoS One. 13, 2, e0192890.

Research output: Contribution to journalArticle

iron overload
Iron Overload
Iron
iron
thalassemia

Sickle cell maculopathy: Identification of systemic risk factors, and microstructural analysis of individual retinal layers of the macula

Dell’Arti, L., Barteselli, G., Riva, L., Carini, E., Graziadei, G., Benatti, E., Invernizzi, A., Cappellini, M. D. & Viola, F., Mar 1 2018, In : PLoS One. 13, 3, e0193582.

Research output: Contribution to journalArticle

sickle cell anemia
Sickle Cell Anemia
Statistical Factor Analysis
risk factors
chelation

Skeletal involvement in type 1 Gaucher disease: Not just bone mineral density

Baldini, M., Casirati, G., Ulivieri, F. M., Cassinerio, E., Khouri Chalouhi, K., Poggiali, E., Borin, L., Burghignoli, V., Cesana, B. M. & Cappellini, M. D., 2018, In : Blood Cells, Molecules, and Diseases. 68, p. 148-152

Research output: Contribution to journalArticle

Gaucher Disease
Bone Density
Spontaneous Fractures
Osteonecrosis
Bone and Bones