• 1974 Citations
  • 13 h-Index
20092019
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Fingerprint Dive into the research topics where Mariapia Cicalese is active. These topic labels come from the works of this person. Together they form a unique fingerprint.

  • 20 Similar Profiles
Genetic Therapy Medicine & Life Sciences
Cell- and Tissue-Based Therapy Medicine & Life Sciences
Hematopoietic Stem Cells Medicine & Life Sciences
Wiskott-Aldrich Syndrome Medicine & Life Sciences
Metachromatic Leukodystrophy Medicine & Life Sciences
Adenosine Deaminase Medicine & Life Sciences
Mutation Medicine & Life Sciences
Severe Combined Immunodeficiency Medicine & Life Sciences

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Research Output 2009 2019

  • 1974 Citations
  • 13 h-Index
  • 47 Article
  • 1 Letter
18 Citations (Scopus)

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Marktel, S., Scaramuzza, S., Cicalese, M. P., Giglio, F., Galimberti, S., Lidonnici, M. R., Calbi, V., Assanelli, A., Bernardo, M. E., Rossi, C., Calabria, A., Milani, R., Gattillo, S., Benedicenti, F., Spinozzi, G., Aprile, A., Bergami, A., Casiraghi, M., Consiglieri, G., Masera, N. & 18 others, D’Angelo, E., Mirra, N., Origa, R., Tartaglione, I., Perrotta, S., Winter, R., Coppola, M., Viarengo, G., Santoleri, L., Graziadei, G., Gabaldo, M., Valsecchi, M. G., Montini, E., Naldini, L., Cappellini, M. D., Ciceri, F., Aiuti, A. & Ferrari, G., Jan 1 2019, (Accepted/In press) In : Nature Medicine.

Research output: Contribution to journalArticle

Gene therapy
Pediatrics
Thalassemia
Cell- and Tissue-Based Therapy
Hematopoietic Stem Cells

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Marktel, S., Scaramuzza, S., Cicalese, M. P., Giglio, F., Galimberti, S., Lidonnici, M. R., Calbi, V., Assanelli, A., Bernardo, M. E., Rossi, C., Calabria, A., Milani, R., Gattillo, S., Benedicenti, F., Spinozzi, G., Aprile, A., Bergami, A., Casiraghi, M., Consiglieri, G., Masera, N. & 18 others, D’Angelo, E., Mirra, N., Origa, R., Tartaglione, I., Perrotta, S., Winter, R., Coppola, M., Viarengo, G., Santoleri, L., Graziadei, G., Gabaldo, M., Valsecchi, M. G., Montini, E., Naldini, L., Cappellini, M. D., Ciceri, F., Aiuti, A. & Ferrari, G., 2019, In : Nature Medicine. 25, 2, p. 234-241 8 p.

Research output: Contribution to journalArticle

8 Citations (Scopus)

Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study

Ferrua, F., Cicalese, M. P., Galimberti, S., Giannelli, S., Dionisio, F., Barzaghi, F., Migliavacca, M., Bernardo, M. E., Calbi, V., Assanelli, A. A., Facchini, M., Fossati, C., Albertazzi, E., Scaramuzza, S., Brigida, I., Scala, S., Basso-Ricci, L., Pajno, R., Casiraghi, M., Canarutto, D. & 18 others, Salerio, F. A., Albert, M. H., Bartoli, A., Wolf, H. M., Fiori, R., Silvani, P., Gattillo, S., Villa, A., Biasco, L., Dott, C., Culme-Seymour, E. J., van Rossem, K., Atkinson, G., Valsecchi, M. G., Roncarolo, M. G., Ciceri, F., Naldini, L. & Aiuti, A., May 1 2019, In : The Lancet Haematology. 6, 5, p. e239-e253

Research output: Contribution to journalArticle

Open Access
Wiskott-Aldrich Syndrome
Cell- and Tissue-Based Therapy
Genetic Therapy
Stem Cells
Wiskott-Aldrich Syndrome Protein
4 Citations (Scopus)

Circulating follicular helper and follicular regulatory T cells are severely compromised in human CD40 deficiency: A case report

Cicalese, M. P., Gerosa, J., Baronio, M., Montin, D., Licciardi, F., Soresina, A., Dellepiane, R. M., Miano, M., Baselli, L. A., Volpi, S., Dufour, C., Plebani, A., Aiuti, A., Lougaris, V. & Fousteri, G., Aug 6 2018, In : Frontiers in Immunology. 9, AUG, 1761.

Research output: Contribution to journalArticle

Hyper-IgM Immunodeficiency Syndrome
Regulatory T-Lymphocytes
Mutation
CD40 Ligand
Germinal Center

Circulating follicular helper and follicular regulatory T cells are severely compromised in human CD40 deficiency: A case report

Cicalese, MP., Gerosa, J., Baronio, M., Montin, D., Licciardi, F., Soresina, A., Dellepiane, RM., Miano, M., Baselli, LA., Volpi, S., Dufour, C., Plebani, A., Aiuti, A., Lougaris, V. & Fousteri, G., 2018, In : Frontiers in Immunology. 9, 1761.

Research output: Contribution to journalArticle

Hyper-IgM Immunodeficiency Syndrome
Regulatory T-Lymphocytes
Mutation
CD40 Ligand
Germinal Center