• 2505 Citations
  • 19 h-Index
20042019
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Fingerprint Dive into the research topics where Samantha Scaramuzza is active. These topic labels come from the works of this person. Together they form a unique fingerprint.

  • 23 Similar Profiles
Wiskott-Aldrich Syndrome Medicine & Life Sciences
Genetic Therapy Medicine & Life Sciences
Hematopoietic Stem Cells Medicine & Life Sciences
Cell- and Tissue-Based Therapy Medicine & Life Sciences
Adenosine Deaminase Medicine & Life Sciences
B-Lymphocytes Medicine & Life Sciences
Wiskott-Aldrich Syndrome Protein Medicine & Life Sciences
T-Lymphocytes Medicine & Life Sciences

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Research Output 2004 2019

  • 2505 Citations
  • 19 h-Index
  • 35 Article
  • 2 Comment/debate
3 Citations (Scopus)
Open Access
Thalassemia
Mesenchymal Stromal Cells
Bone Marrow
Iron Overload
Hematopoietic Stem Cells
18 Citations (Scopus)

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Marktel, S., Scaramuzza, S., Cicalese, M. P., Giglio, F., Galimberti, S., Lidonnici, M. R., Calbi, V., Assanelli, A., Bernardo, M. E., Rossi, C., Calabria, A., Milani, R., Gattillo, S., Benedicenti, F., Spinozzi, G., Aprile, A., Bergami, A., Casiraghi, M., Consiglieri, G., Masera, N. & 18 others, D’Angelo, E., Mirra, N., Origa, R., Tartaglione, I., Perrotta, S., Winter, R., Coppola, M., Viarengo, G., Santoleri, L., Graziadei, G., Gabaldo, M., Valsecchi, M. G., Montini, E., Naldini, L., Cappellini, M. D., Ciceri, F., Aiuti, A. & Ferrari, G., Jan 1 2019, (Accepted/In press) In : Nature Medicine.

Research output: Contribution to journalArticle

Gene therapy
Pediatrics
Thalassemia
Cell- and Tissue-Based Therapy
Hematopoietic Stem Cells

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Marktel, S., Scaramuzza, S., Cicalese, M. P., Giglio, F., Galimberti, S., Lidonnici, M. R., Calbi, V., Assanelli, A., Bernardo, M. E., Rossi, C., Calabria, A., Milani, R., Gattillo, S., Benedicenti, F., Spinozzi, G., Aprile, A., Bergami, A., Casiraghi, M., Consiglieri, G., Masera, N. & 18 others, D’Angelo, E., Mirra, N., Origa, R., Tartaglione, I., Perrotta, S., Winter, R., Coppola, M., Viarengo, G., Santoleri, L., Graziadei, G., Gabaldo, M., Valsecchi, M. G., Montini, E., Naldini, L., Cappellini, M. D., Ciceri, F., Aiuti, A. & Ferrari, G., 2019, In : Nature Medicine. 25, 2, p. 234-241 8 p.

Research output: Contribution to journalArticle

8 Citations (Scopus)

Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study

Ferrua, F., Cicalese, M. P., Galimberti, S., Giannelli, S., Dionisio, F., Barzaghi, F., Migliavacca, M., Bernardo, M. E., Calbi, V., Assanelli, A. A., Facchini, M., Fossati, C., Albertazzi, E., Scaramuzza, S., Brigida, I., Scala, S., Basso-Ricci, L., Pajno, R., Casiraghi, M., Canarutto, D. & 18 others, Salerio, F. A., Albert, M. H., Bartoli, A., Wolf, H. M., Fiori, R., Silvani, P., Gattillo, S., Villa, A., Biasco, L., Dott, C., Culme-Seymour, E. J., van Rossem, K., Atkinson, G., Valsecchi, M. G., Roncarolo, M. G., Ciceri, F., Naldini, L. & Aiuti, A., May 1 2019, In : The Lancet Haematology. 6, 5, p. e239-e253

Research output: Contribution to journalArticle

Open Access
Wiskott-Aldrich Syndrome
Cell- and Tissue-Based Therapy
Genetic Therapy
Stem Cells
Wiskott-Aldrich Syndrome Protein

A novel genomic inversion in Wiskott-Aldrich-associated autoinflammation

Brigida, I., Scaramuzza, S., Lazarevic, D., Cittaro, D., Ferrua, F., Leonardelli, L., Alessio, M., Forma, O., Lanzani, C., Viarengo, G., Ciceri, F., Jankovic, M., Pesce, F., Aiuti, A. & Cicalese, M., 2016, (Accepted/In press) In : Journal of Allergy and Clinical Immunology.

Research output: Contribution to journalArticle