A 5-center experience with intrathecal administration of nusinersen in SMA1 in Italy letter to the editor of european journal of pediatric neurology regarding the manuscript “single-center experience with intrathecal administration of nusinersen in children with spinal muscular atrophy type 1” written by pechmann and colleagues”

V.A. Sansone, M. Pane, S. Messina, C. Bruno, A. D'Amico, E. Albamonte, M. Catteruccia, M. Sframeli, M. Pedemonte, G. Vita, E. Bertini, E. Mercuri, D. Leone, R. de Sanctis, N. Forcina, M. Piastra, O. Genovese, A. Pedicelli, A. Versaci, I. RulliE. Gitto, C. Faraone, S. La Foresta, M. Macrì, G. Colia, A.M. Bonetti, A. Carlesi, R. Cutrera, M.B. Chiarini, M. Ferretti, A. Garaventa, G. Montobbio, C. Gandolfo, V. Iurilli, P. Tacchetti, E. Bobeica, A. D'Agostino, A. Pirola, S. Lupone, E. De Mattia, E. Falcier, F. Rao, J. Casiraghi, F. Salmin, C. Grandi, F. Fedeli, L. Mancini, P. Stoia, M. Heinen, V. Cozzi

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)729-731
Number of pages3
JournalEuropean Journal of Paediatric Neurology
Volume22
Issue number4
DOIs
Publication statusPublished - 2018

Keywords

  • nusinersen
  • oligonucleotide, child
  • human
  • Italy
  • Letter
  • lumbar puncture
  • pediatrics
  • priority journal
  • Werdnig Hoffmann disease
  • hereditary spinal muscular atrophy
  • neurology
  • spinal muscular atrophy, Child
  • Humans
  • Muscular Atrophy, Spinal
  • Neurology
  • Oligonucleotides
  • Spinal Muscular Atrophies of Childhood

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