Cell based therapy for duchenne muscular dystrophy

Andrea Farini, Paola Razini, Silvia Erratico, Yvan Torrente, Mirella Meregalli

Research output: Contribution to journalArticlepeer-review


Mutations in the dystrophin gene cause an X-linked genetic disorder: Duchenne muscular dystrophy (DMD). Stem cell therapy is an attractive method to treat DMD because a small number of cells are required to obtain a therapeutic effect. Here, we discussed about multiple types of myogenic stem cells and their possible use to treat DMD. The identification of a stem cell population providing efficient muscle regeneration is critical for the progression of cell therapy for DMD. We speculated that the most promising possibility for the treatment of DMD is a combination of different approaches, such as gene and stem cell therapy.

Original languageEnglish
Pages (from-to)526-534
Number of pages9
JournalJournal of Cellular Physiology
Issue number3
Publication statusPublished - Dec 2009

ASJC Scopus subject areas

  • Clinical Biochemistry
  • Cell Biology
  • Physiology


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