Cost-effectiveness analysis and prevention effects of ultra-orphan drugs for rare diseases: An in silico model applied to Cryopyrin Associated Periodic Syndromes (CAPS)

L. Trieste, O. Della Casa Alberighi, G. Turchetti, F. Pierotti, L. Accame, V. Lorenzoni, J. Frenkel, M. Gattorno, P. Quartier, A. Martini

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Article numberP185
JournalPediatric Rheumatology
Issue number1
Publication statusPublished - Sep 28 2015

ASJC Scopus subject areas

  • Rheumatology
  • Immunology and Allergy
  • Pediatrics, Perinatology, and Child Health

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