Defining orphan conditions in the context of the European orphan regulation: challenges and evolution

Daniel J O'Connor, Maria E Sheean, Matthias P Hofer, Stelios Tsigkos, Segundo Mariz, Laura Fregonese, Kristina Larsson, Virginie Hivert, Kerstin Westermark, Frauke Naumann-Winter, Violeta Stoyanova-Beninska, Ingeborg Barišić, Giuseppe Capovilla, Armando Magrelli, Bruno Sepodes

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)479-480
Number of pages2
JournalNature Reviews Drug Discovery
Volume18
Issue number7
DOIs
Publication statusPublished - Jul 2019

Keywords

  • Drug Development/methods
  • European Union
  • Government Regulation
  • Humans
  • Legislation, Drug
  • Orphan Drug Production/legislation & jurisprudence
  • Rare Diseases/diagnosis

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