Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience

Sonia Messina, Marika Pane, Valeria Sansone, Claudio Bruno, Michela Catteruccia, Giuseppe Vita, Concetta Palermo, Emilio Albamonte, Marina Pedemonte, Enrico Bertini, Luca Binetti, Eugenio Mercuri, Daniela Lauro, Anita Pallara, Simona Spinoglio, Maria Letizia Solinas, Grazia Zappa, Francesca Penno, Cristina Ponzanelli, Jacopo CasiraghiMarcello Villanova, Danilo Tiziano, Anna Mandelli, Chiara Mastella, Alberto Fontana, Anna Ambrosini, Daniela Leone, Roberto de Sanctis, Nicola Forcina, Marco Piastra, Orazio Genovese, Alessandro Pedicelli, Maria Sframeli, Antonio Versaci, Imma Rulli, Eloisa Gitto, Cristina Faraone, Stefania La Foresta, Maria Macrì, Adele D'Amico, Giulia Colia, Anna Maria Bonetti, Adelina Carlesi, Renato Cutrera, Maria Beatrice Chiarini, Marta Ferretti, Alberto Garaventa, Giovanni Montobbio, Carlo Gandolfo, Valentina Iurilli, on behalf of the Italian EAP working Group

Research output: Contribution to journalEditorialpeer-review

Original languageEnglish
Pages (from-to)1084-1086
Number of pages3
JournalNeuromuscular Disorders
Volume27
Issue number12
DOIs
Publication statusPublished - Dec 1 2017

ASJC Scopus subject areas

  • Pediatrics, Perinatology, and Child Health
  • Neurology
  • Clinical Neurology
  • Genetics(clinical)

Cite this