Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience

Sonia Messina, Marika Pane, Valeria Sansone, Claudio Bruno, Michela Catteruccia, Giuseppe Vita, Concetta Palermo, Emilio Albamonte, Marina Pedemonte, Enrico Bertini, Luca Binetti, Eugenio Mercuri, Italian EAP working Group, Anna Ambrosini

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)1084-1086
Number of pages3
JournalNeuromuscular Disorders
Issue number12
Publication statusPublished - Dec 1 2017


  • Editorial

Cite this