Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience

Sonia Messina; Marika Pane; Valeria Sansone; Claudio Bruno; Michela Catteruccia; Giuseppe Vita; Concetta Palermo; Emilio Albamonte; Marina Pedemonte; Enrico Bertini; Luca Binetti; Eugenio Mercuri; Italian EAP working Group; Anna Ambrosini

doi:10.1016/j.nmd.2017.09.006

Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience

Sonia Messina, Marika Pane, Valeria Sansone, Claudio Bruno, Michela Catteruccia, Giuseppe Vita, Concetta Palermo, Emilio Albamonte, Marina Pedemonte, Enrico Bertini, Luca Binetti, Eugenio Mercuri, Italian EAP working Group, Anna Ambrosini

Research output: Contribution to journal › Article › peer-review

Original language	English
Pages (from-to)	1084-1086
Number of pages	3
Journal	Neuromuscular Disorders
Volume	27
Issue number	12
DOIs	https://doi.org/10.1016/j.nmd.2017.09.006
Publication status	Published - Dec 1 2017

Keywords

Editorial

Access to Document

10.1016/j.nmd.2017.09.006

Cite this

Messina, S., Pane, M., Sansone, V., Bruno, C., Catteruccia, M., Vita, G., Palermo, C., Albamonte, E., Pedemonte, M., Bertini, E., Binetti, L., Mercuri, E., Group, I. EAP. W., & Ambrosini, A. (2017). Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience. Neuromuscular Disorders, 27(12), 1084-1086. https://doi.org/10.1016/j.nmd.2017.09.006

Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience. / Messina, Sonia; Pane, Marika; Sansone, Valeria; Bruno, Claudio ; Catteruccia, Michela; Vita, Giuseppe; Palermo, Concetta; Albamonte, Emilio; Pedemonte, Marina ; Bertini, Enrico; Binetti, Luca; Mercuri, Eugenio; Group, Italian EAP working; Ambrosini, Anna.

In: Neuromuscular Disorders, Vol. 27, No. 12, 01.12.2017, p. 1084-1086.

Research output: Contribution to journal › Article › peer-review

Messina, S, Pane, M, Sansone, V, Bruno, C , Catteruccia, M, Vita, G, Palermo, C, Albamonte, E, Pedemonte, M , Bertini, E, Binetti, L, Mercuri, E, Group, IEAPW & Ambrosini, A 2017, 'Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience', Neuromuscular Disorders, vol. 27, no. 12, pp. 1084-1086. https://doi.org/10.1016/j.nmd.2017.09.006

Messina, Sonia ; Pane, Marika ; Sansone, Valeria ; Bruno, Claudio ; Catteruccia, Michela ; Vita, Giuseppe ; Palermo, Concetta ; Albamonte, Emilio ; Pedemonte, Marina ; Bertini, Enrico ; Binetti, Luca ; Mercuri, Eugenio ; Group, Italian EAP working ; Ambrosini, Anna. / Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience. In: Neuromuscular Disorders. 2017 ; Vol. 27, No. 12. pp. 1084-1086.

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