In vitro restoration of functional SMN protein in human trophoblast cells affected by spinal muscular atrophy by small fragment homologous replacement

Federica Sangiuolo, Antonio Filareto, Paola Spitalieri, Maria Lucia Scaldaferri, Ruggiero Mango, Emanuela Bruscia, Gennaro Citro, Ercole Brunetti, Massimo De Felici, Giuseppe Novelli

Research output: Contribution to journalArticle

Fingerprint Dive into the research topics of 'In vitro restoration of functional SMN protein in human trophoblast cells affected by spinal muscular atrophy by small fragment homologous replacement'. Together they form a unique fingerprint.

Medicine & Life Sciences