International Workshop:: Outcome measures and clinical trial readiness in primary mitochondrial myopathies in children and adults. Consensus recommendations. 16–18 November 2016, Rome, Italy

Michelangelo Mancuso; Robert McFarland; Thomas Klopstock; Michio Hirano; Rafael Artuch; Enrico Bertini; Laurence Bindoff; Valerio Carelli; Grainne Gorman; Michio Hirano; Rita Horvath; Petra Kaufmann; Thomas Klopstock; Yasutoshi Koga; Saskia Koene; Costanza Lamperti; Robert McFarland; Michelangelo Mancuso; Julio Montoya; Francisco Javier Pérez-Mínguez Caneda; Vincent Procaccio; Holger Prokisch; Shamima Rahman; Piero Santantonio; Markus Schülke; Serenella Servidei; Dikoma C. Shungu; Gabriele Siciliano; Jan Smeitink; Tanja Taivassalo; John L.P. Thompson; Doug Turnbull; Elja Van der Veer; Philip E. Yeske; Massimo Zeviani; on behalf of the; consortium on Trial Readiness in Mitochondrial Myopathies

doi:10.1016/j.nmd.2017.08.006

International Workshop:: Outcome measures and clinical trial readiness in primary mitochondrial myopathies in children and adults. Consensus recommendations. 16–18 November 2016, Rome, Italy

Michelangelo Mancuso, Robert McFarland, Thomas Klopstock, Michio Hirano, Rafael Artuch, Enrico Bertini, Laurence Bindoff, Valerio Carelli, Grainne Gorman, Michio Hirano, Rita Horvath, Petra Kaufmann, Thomas Klopstock, Yasutoshi Koga, Saskia Koene, Costanza Lamperti, Robert McFarland, Michelangelo Mancuso, Julio Montoya, Francisco Javier Pérez-Mínguez CanedaVincent Procaccio, Holger Prokisch, Shamima Rahman, Piero Santantonio, Markus Schülke, Serenella Servidei, Dikoma C. Shungu, Gabriele Siciliano, Jan Smeitink, Tanja Taivassalo, John L.P. Thompson, Doug Turnbull, Elja Van der Veer, Philip E. Yeske, Massimo Zeviani, on behalf of the, consortium on Trial Readiness in Mitochondrial Myopathies

Research output: Contribution to journal › Article › peer-review

Original language	English
Pages (from-to)	1126-1137
Number of pages	12
Journal	Neuromuscular Disorders
Volume	27
Issue number	12
DOIs	https://doi.org/10.1016/j.nmd.2017.08.006
Publication status	Published - Dec 1 2017

ASJC Scopus subject areas

Pediatrics, Perinatology, and Child Health
Neurology
Clinical Neurology
Genetics(clinical)

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10.1016/j.nmd.2017.08.006

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Mancuso, M., McFarland, R., Klopstock, T., Hirano, M., Artuch, R., Bertini, E., Bindoff, L., Carelli, V., Gorman, G., Hirano, M., Horvath, R., Kaufmann, P., Klopstock, T., Koga, Y., Koene, S., Lamperti, C., McFarland, R., Mancuso, M., Montoya, J., ... consortium on Trial Readiness in Mitochondrial Myopathies (2017). International Workshop:: Outcome measures and clinical trial readiness in primary mitochondrial myopathies in children and adults. Consensus recommendations. 16–18 November 2016, Rome, Italy. Neuromuscular Disorders, 27(12), 1126-1137. https://doi.org/10.1016/j.nmd.2017.08.006

International Workshop:: Outcome measures and clinical trial readiness in primary mitochondrial myopathies in children and adults. Consensus recommendations. 16–18 November 2016, Rome, Italy. / Mancuso, Michelangelo; McFarland, Robert; Klopstock, Thomas; Hirano, Michio; Artuch, Rafael; Bertini, Enrico; Bindoff, Laurence; Carelli, Valerio; Gorman, Grainne; Hirano, Michio; Horvath, Rita; Kaufmann, Petra; Klopstock, Thomas; Koga, Yasutoshi; Koene, Saskia; Lamperti, Costanza; McFarland, Robert; Mancuso, Michelangelo; Montoya, Julio; Javier Pérez-Mínguez Caneda, Francisco; Procaccio, Vincent; Prokisch, Holger; Rahman, Shamima; Santantonio, Piero; Schülke, Markus; Servidei, Serenella; Shungu, Dikoma C.; Siciliano, Gabriele; Smeitink, Jan; Taivassalo, Tanja; Thompson, John L.P.; Turnbull, Doug; Van der Veer, Elja; Yeske, Philip E.; Zeviani, Massimo; on behalf of the; consortium on Trial Readiness in Mitochondrial Myopathies.

In: Neuromuscular Disorders, Vol. 27, No. 12, 01.12.2017, p. 1126-1137.

Research output: Contribution to journal › Article › peer-review

Mancuso, M, McFarland, R, Klopstock, T, Hirano, M, Artuch, R, Bertini, E, Bindoff, L, Carelli, V, Gorman, G, Hirano, M, Horvath, R, Kaufmann, P, Klopstock, T, Koga, Y, Koene, S, Lamperti, C, McFarland, R, Mancuso, M, Montoya, J, Javier Pérez-Mínguez Caneda, F, Procaccio, V, Prokisch, H, Rahman, S, Santantonio, P, Schülke, M, Servidei, S, Shungu, DC, Siciliano, G, Smeitink, J, Taivassalo, T, Thompson, JLP, Turnbull, D, Van der Veer, E, Yeske, PE, Zeviani, M, on behalf of the & consortium on Trial Readiness in Mitochondrial Myopathies 2017, 'International Workshop:: Outcome measures and clinical trial readiness in primary mitochondrial myopathies in children and adults. Consensus recommendations. 16–18 November 2016, Rome, Italy', Neuromuscular Disorders, vol. 27, no. 12, pp. 1126-1137. https://doi.org/10.1016/j.nmd.2017.08.006

Mancuso, Michelangelo ; McFarland, Robert ; Klopstock, Thomas ; Hirano, Michio ; Artuch, Rafael ; Bertini, Enrico ; Bindoff, Laurence ; Carelli, Valerio ; Gorman, Grainne ; Hirano, Michio ; Horvath, Rita ; Kaufmann, Petra ; Klopstock, Thomas ; Koga, Yasutoshi ; Koene, Saskia ; Lamperti, Costanza ; McFarland, Robert ; Mancuso, Michelangelo ; Montoya, Julio ; Javier Pérez-Mínguez Caneda, Francisco ; Procaccio, Vincent ; Prokisch, Holger ; Rahman, Shamima ; Santantonio, Piero ; Schülke, Markus ; Servidei, Serenella ; Shungu, Dikoma C. ; Siciliano, Gabriele ; Smeitink, Jan ; Taivassalo, Tanja ; Thompson, John L.P. ; Turnbull, Doug ; Van der Veer, Elja ; Yeske, Philip E. ; Zeviani, Massimo ; on behalf of the ; consortium on Trial Readiness in Mitochondrial Myopathies. / International Workshop:: Outcome measures and clinical trial readiness in primary mitochondrial myopathies in children and adults. Consensus recommendations. 16–18 November 2016, Rome, Italy. In: Neuromuscular Disorders. 2017 ; Vol. 27, No. 12. pp. 1126-1137.

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AU - Artuch, Rafael

AU - Bertini, Enrico

AU - Bindoff, Laurence

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AU - Procaccio, Vincent

AU - Prokisch, Holger

AU - Rahman, Shamima

AU - Santantonio, Piero

AU - Schülke, Markus

AU - Servidei, Serenella

AU - Shungu, Dikoma C.

AU - Siciliano, Gabriele

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International Workshop:: Outcome measures and clinical trial readiness in primary mitochondrial myopathies in children and adults. Consensus recommendations. 16–18 November 2016, Rome, Italy

ASJC Scopus subject areas

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