Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study: The Lancet Haematology

F Ferrua, MP Cicalese, S Galimberti, S Giannelli, F Dionisio, F Barzaghi, M Migliavacca, ME Bernardo, V Calbi, AA Assanelli, M Facchini, C Fossati, E Albertazzi, S Scaramuzza, I Brigida, S Scala, L Basso-Ricci, R Pajno, M Casiraghi, D CanaruttoFA Salerio, MH Albert, A Bartoli, HM Wolf, R Fiori, P Silvani, S Gattillo, A Villa, L Biasco, C Dott, EJ Culme-Seymour, K van Rossem, G Atkinson, MG Valsecchi, MG Roncarolo, F Ciceri, L Naldini, A Aiuti

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