Nusinersen treatment and cerebrospinal fluid neurofilaments: An explorative study on Spinal Muscular Atrophy type 3 patients

I. Faravelli, M. Meneri, D. Saccomanno, D. Velardo, E. Abati, D. Gagliardi, V. Parente, L. Petrozzi, D. Ronchi, N. Stocchetti, E. Calderini, G. D’Angelo, G. Chidini, E. Prandi, G. Ricci, G. Siciliano, N. Bresolin, G.P. Comi, S. Corti, F. MagriA. Govoni

Research output: Contribution to journalArticle

Original languageEnglish
Pages (from-to)3034-3039
Number of pages6
JournalJOURNAL OF CELLULAR AND MOLECULAR MEDICINE
Volume24
Issue number5
DOIs
Publication statusPublished - 2020

Keywords

  • neurofilaments
  • Nusinersen
  • pharmacodynamics biomarker
  • spinal muscular atrophy
  • neurofilament protein
  • nusinersen
  • aged
  • Article
  • biochemical analysis
  • cerebrospinal fluid
  • cerebrospinal fluid analysis
  • child
  • clinical article
  • clinical assessment
  • controlled study
  • disease duration
  • enzyme linked immunosorbent assay
  • exploratory research
  • female
  • follow up
  • Hammersmith Functional Motor Scale Expanded
  • human
  • Kugelberg Welander disease
  • limit of quantitation
  • male
  • motor function test
  • motor performance
  • nerve fiber degeneration
  • neurofilament
  • priority journal
  • psychosomatic disorder
  • scoring system
  • six minute walk test
  • treatment response

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